The HIBISCUS-KIDS Study: A single-arm, open-label, phase 1/2 study to evaluate the pharmacokinetics and safety of etavopivat in pediatric patients with sickle cell disease
Raffaella Colombatti1; Julie Kanter2; Miguel R. Abboud3; Eric Wu4; Leila Jerome Clay4; Andrew Campbell5; Adlette Inati6
Poster
Saturday, 28 October 2023
09:00 - 11:15
BST
ORAL PRESENTATION
ASCENT1 (trial in progress): A phase 2 trial to evaluate the efficacy and safety of oral decitabine–tetrahydrouridine (NDec) in patients with sickle cell disease