Padua
,
Italy
12 - 14 September 2025
Bari International Congress (BIC 2025)
Presentation schedule and materials
Friday, 12 September 2025
09:20
- 09:40
CET
ORAL PRESENTATION
Oral factor VIII (FVIII) bispecific for haemophilia A
Jan Astermark1
MATERIALS AVAILABLE
17:00
- 17:10
CET
ORAL PRESENTATION
Endonuclease-mediated genomic insertion of AAV-delivered FVIII transgene into hepatocyte safe-harbor locus restores durable FVIII activity in vivo
Jacob Lund1; Carsten Dan Ley1; Karl Agger2; Christopher William Smith1; Jesper Tranekjær Jørgensen1; Michelle Scalley Kim2; Jazz Hallinan2; Kendall Sanson2; Rikke Hvid Lindecrona3; Lene Diness Jensen3; Nadin Jahnke2; Gert Bolt2; Erin Louise Brown2; Jonas Ahnfelt-Rønne3; Esther Bloem2; Jonas Højfeldt2; Karina Thorn2 and Gro Klitgaard Povlsen1
MATERIALS AVAILABLE
Keywords